Gene editing strategies to treat lysosomal disorders: The example of mucopolysaccharidoses
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Title
Gene editing strategies to treat lysosomal disorders: The example of mucopolysaccharidoses
Authors
Keywords
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Journal
ADVANCED DRUG DELIVERY REVIEWS
Volume 191, Issue -, Pages 114616
Publisher
Elsevier BV
Online
2022-11-08
DOI
10.1016/j.addr.2022.114616
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