Human genome-edited hematopoietic stem cells phenotypically correct Mucopolysaccharidosis type I
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Title
Human genome-edited hematopoietic stem cells phenotypically correct Mucopolysaccharidosis type I
Authors
Keywords
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Journal
Nature Communications
Volume 10, Issue 1, Pages -
Publisher
Springer Science and Business Media LLC
Online
2019-09-06
DOI
10.1038/s41467-019-11962-8
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