Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation
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Title
Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation
Authors
Keywords
mucopolysaccharidosis type II, bone lineage, bone mineral density, bone strength, ex vivo, gene therapy, lentivirus, hematopoietic stem cell, Hunter disease, osteoclast, osteoblast
Journal
Molecular Therapy-Methods & Clinical Development
Volume 19, Issue -, Pages 261-274
Publisher
Elsevier BV
Online
2020-09-20
DOI
10.1016/j.omtm.2020.09.012
References
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