In utero adenine base editing corrects multi-organ pathology in a lethal lysosomal storage disease
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Title
In utero adenine base editing corrects multi-organ pathology in a lethal lysosomal storage disease
Authors
Keywords
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Journal
Nature Communications
Volume 12, Issue 1, Pages -
Publisher
Springer Science and Business Media LLC
Online
2021-07-13
DOI
10.1038/s41467-021-24443-8
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