Lung-selective mRNA delivery of synthetic lipid nanoparticles for the treatment of pulmonary lymphangioleiomyomatosis
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Title
Lung-selective mRNA delivery of synthetic lipid nanoparticles for the treatment of pulmonary lymphangioleiomyomatosis
Authors
Keywords
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Journal
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Volume 119, Issue 8, Pages e2116271119
Publisher
Proceedings of the National Academy of Sciences
Online
2022-02-17
DOI
10.1073/pnas.2116271119
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Note: Only part of the references are listed.- Lipid nanoparticle-mediated codelivery of Cas9 mRNA and single-guide RNA achieves liver-specific in vivo genome editing of Angptl3
- (2021) Min Qiu et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Vitamin lipid nanoparticles enable adoptive macrophage transfer for the treatment of multidrug-resistant bacterial sepsis
- (2020) Xucheng Hou et al. Nature Nanotechnology
- Engineering Caveolae-Targeted Lipid Nanoparticles To Deliver mRNA to the Lungs
- (2020) Qing Li et al. ACS Chemical Biology
- Selective organ targeting (SORT) nanoparticles for tissue-specific mRNA delivery and CRISPR–Cas gene editing
- (2020) Qiang Cheng et al. Nature Nanotechnology
- Imidazole‐based Synthetic Lipidoids for In Vivo mRNA Delivery into Primary T Lymphocytes
- (2020) Xuewei Zhao et al. ANGEWANDTE CHEMIE-INTERNATIONAL EDITION
- An RNA vaccine drives immunity in checkpoint-inhibitor-treated melanoma
- (2020) Ugur Sahin et al. NATURE
- Neurotransmitter-derived lipidoids (NT-lipidoids) for enhanced brain delivery through intravenous injection
- (2020) Feihe Ma et al. Science Advances
- Functionalized lipid-like nanoparticles for in vivo mRNA delivery and base editing
- (2020) Xinfu Zhang et al. Science Advances
- A Systematic Study of Unsaturation in Lipid Nanoparticles Leads to Improved mRNA Transfection In Vivo
- (2020) Sang Lee et al. ANGEWANDTE CHEMIE-INTERNATIONAL EDITION
- Branched-Tail Lipid Nanoparticles Potently Deliver mRNA In Vivo due to Enhanced Ionization at Endosomal pH
- (2019) Khalid A. Hajj et al. Small
- Genome Editing with mRNA Encoding ZFN, TALEN, and Cas9
- (2019) Hong-Xia Zhang et al. MOLECULAR THERAPY
- mRNA as a Transformative Technology for Vaccine Development to Control Infectious Diseases
- (2019) Giulietta Maruggi et al. MOLECULAR THERAPY
- Delivering the Messenger: Advances in Technologies for Therapeutic mRNA Delivery
- (2019) Piotr S. Kowalski et al. MOLECULAR THERAPY
- mRNA vaccines against H10N8 and H7N9 influenza viruses of pandemic potential are immunogenic and well tolerated in healthy adults in phase 1 randomized clinical trials
- (2019) Robert A. Feldman et al. VACCINE
- Fast and Efficient CRISPR/Cas9 Genome Editing In Vivo Enabled by Bioreducible Lipid and Messenger RNA Nanoparticles
- (2019) Ji Liu et al. ADVANCED MATERIALS
- Targeting mTOR for cancer therapy
- (2019) Hui Hua et al. Journal of Hematology & Oncology
- Constrained Nanoparticles Deliver siRNA and sgRNA to T Cells In Vivo without Targeting Ligands
- (2019) Melissa P. Lokugamage et al. ADVANCED MATERIALS
- Delivery of mRNA vaccines with heterocyclic lipids increases anti-tumor efficacy by STING-mediated immune cell activation
- (2019) Lei Miao et al. NATURE BIOTECHNOLOGY
- Brain-targeted drug delivery by manipulating protein corona functions
- (2019) Zui Zhang et al. Nature Communications
- The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs
- (2019) Akin Akinc et al. Nature Nanotechnology
- Pulmonary vascular endothelium: the orchestra conductor in respiratory diseases
- (2018) Alice Huertas et al. EUROPEAN RESPIRATORY JOURNAL
- A Novel Amino Lipid Series for mRNA Delivery: Improved Endosomal Escape and Sustained Pharmacology and Safety in Non-human Primates
- (2018) Staci Sabnis et al. MOLECULAR THERAPY
- Lipid Nanoparticle Formulations for Enhanced Co-delivery of siRNA and mRNA
- (2018) Rebecca L. Ball et al. NANO LETTERS
- A modular platform for targeted RNAi therapeutics
- (2018) Ranit Kedmi et al. Nature Nanotechnology
- mRNA vaccines — a new era in vaccinology
- (2018) Norbert Pardi et al. NATURE REVIEWS DRUG DISCOVERY
- Multi-antigenic human cytomegalovirus mRNA vaccines that elicit potent humoral and cell-mediated immunity
- (2018) Shinu John et al. VACCINE
- Enhanced efficacy of combined temozolomide and bromodomain inhibitor therapy for gliomas using targeted nanoparticles
- (2018) Fred C. Lam et al. Nature Communications
- Rapid, Single-Cell Analysis and Discovery of Vectored mRNA Transfection In Vivo with a loxP-Flanked tdTomato Reporter Mouse
- (2018) Kevin J. Kauffman et al. Molecular Therapy-Nucleic Acids
- Immune Checkpoint Ligand PD-L1 is Upregulated in Pulmonary Lymphangioleiomyomatosis (LAM)
- (2018) Katharina Maisel et al. AMERICAN JOURNAL OF RESPIRATORY CELL AND MOLECULAR BIOLOGY
- An RNA toolbox for cancer immunotherapy
- (2018) Fernando Pastor et al. NATURE REVIEWS DRUG DISCOVERY
- Intracellular delivery and biodistribution study of CRISPR/Cas9 ribonucleoprotein loaded bioreducible lipidoid nanoparticles
- (2018) Yamin Li et al. Biomaterials Science
- Dendrimer-Based Lipid Nanoparticles Deliver Therapeutic FAH mRNA to Normalize Liver Function and Extend Survival in a Mouse Model of Hepatorenal Tyrosinemia Type I
- (2018) Qiang Cheng et al. ADVANCED MATERIALS
- The Crown and the Scepter: Roles of the Protein Corona in Nanomedicine
- (2018) Rong Cai et al. ADVANCED MATERIALS
- Cloaking nanoparticles with protein corona shield for targeted drug delivery
- (2018) Jun Yong Oh et al. Nature Communications
- Tools for translation: non-viral materials for therapeutic mRNA delivery
- (2017) Khalid A. Hajj et al. Nature Reviews Materials
- Non-Viral CRISPR/Cas Gene Editing In Vitro and In Vivo Enabled by Synthetic Nanoparticle Co-Delivery of Cas9 mRNA and sgRNA
- (2016) Jason B. Miller et al. ANGEWANDTE CHEMIE-INTERNATIONAL EDITION
- Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system
- (2016) F DeRosa et al. GENE THERAPY
- Efficient delivery of genome-editing proteins using bioreducible lipid nanoparticles
- (2016) Ming Wang et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Corona-Directed Nucleic Acid Delivery into Hepatic Stellate Cells for Liver Fibrosis Therapy
- (2015) Zhengping Zhang et al. ACS Nano
- Cystic fibrosis airway epithelium remodelling: involvement of inflammation
- (2014) Damien Adam et al. JOURNAL OF PATHOLOGY
- mRNA-based therapeutics — developing a new class of drugs
- (2014) Ugur Sahin et al. NATURE REVIEWS DRUG DISCOVERY
- Rapid formation of plasma protein corona critically affects nanoparticle pathophysiology
- (2013) Stefan Tenzer et al. Nature Nanotechnology
- Control of Anti-Thrombogenic Properties: Surface-Induced Self-Assembly of Fibrinogen Fibers
- (2012) Jaseung Koo et al. BIOMACROMOLECULES
- Prevention of Alveolar Destruction and Airspace Enlargement in a Mouse Model of Pulmonary Lymphangioleiomyomatosis (LAM)
- (2012) E. A. Goncharova et al. Science Translational Medicine
- A Combinatorial Library of Unsaturated Lipidoids for Efficient Intracellular Gene Delivery
- (2012) Ming Wang et al. ACS Synthetic Biology
- Physical−Chemical Aspects of Protein Corona: Relevance toin Vitroandin VivoBiological Impacts of Nanoparticles
- (2011) Marco P. Monopoli et al. JOURNAL OF THE AMERICAN CHEMICAL SOCIETY
- Efficacy and Safety of Sirolimus in Lymphangioleiomyomatosis
- (2011) NEW ENGLAND JOURNAL OF MEDICINE
- Efficacy and Safety of Sirolimus in Lymphangioleiomyomatosis
- (2011) Francis X. McCormack et al. NEW ENGLAND JOURNAL OF MEDICINE
- Evaluation of fibrinogen self-assembly: role of its αC region
- (2010) J. KOO et al. JOURNAL OF THROMBOSIS AND HAEMOSTASIS
- Sirolimus for Angiomyolipoma in Tuberous Sclerosis Complex or Lymphangioleiomyomatosis
- (2008) John J. Bissler et al. NEW ENGLAND JOURNAL OF MEDICINE
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