Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system
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Title
Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system
Authors
Keywords
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Journal
GENE THERAPY
Volume 23, Issue 10, Pages 699-707
Publisher
Springer Nature
Online
2016-06-30
DOI
10.1038/gt.2016.46
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