IntraneuralGJB1gene delivery improves nerve pathology in a model of X-linked Charcot-Marie-Tooth disease

Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy

(2014) A. Lattanzi et al.   HUMAN MOLECULAR GENETICS

In vivo introduction of transgenes into mouse sciatic nerve cells in situ using viral vectors

(2014) Sergio Gonzalez et al.   Nature Protocols

AAV1.NT-3 Gene Therapy for Charcot–Marie–Tooth Neuropathy

(2013) Zarife Sahenk et al.   MOLECULAR THERAPY

Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy

(2013) A. Biffi et al.   SCIENCE

How do mutations in GJB1 cause X-linked Charcot–Marie–Tooth disease?

(2012) Kleopas A. Kleopa et al.   BRAIN RESEARCH

Myelination in coculture of established neuronal and Schwann cell lines

(2012) Kazunori Sango et al.   HISTOCHEMISTRY AND CELL BIOLOGY

Lentiviral vector common integration sites in preclinical models and a clinical trial reflect a benign integration bias and not oncogenic selection

(2011) A. Biffi et al.   BLOOD

Schwann cell targeting via intrasciatic injection of AAV8 as gene therapy strategy for peripheral nerve regeneration

(2011) J Homs et al.   GENE THERAPY

The Role of Gap Junctions in Charcot-Marie-Tooth Disease

(2011) K. A. Kleopa   JOURNAL OF NEUROSCIENCE

Widespread enzymatic correction of CNS tissues by a single intracerebral injection of therapeutic lentiviral vector in leukodystrophy mouse models

(2010) Annalisa Lattanzi et al.   HUMAN MOLECULAR GENETICS

Axonal Pathology Precedes Demyelination in a Mouse Model of X-Linked Demyelinating/Type I Charcot-Marie Tooth Neuropathy

(2010) Natalie Vavlitou et al.   JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY

Pals1 Is a Major Regulator of the Epithelial-Like Polarization and the Extension of the Myelin Sheath in Peripheral Nerves

(2010) M. Ozcelik et al.   JOURNAL OF NEUROSCIENCE

Dlg1-PTEN Interaction Regulates Myelin Thickness to Prevent Damaging Peripheral Nerve Overmyelination

(2010) L. Cotter et al.   SCIENCE

Induction of Myelin Protein Zero by Early Growth Response 2 through Upstream and Intragenic Elements

(2009) Sung-Wook Jang et al.   JOURNAL OF BIOLOGICAL CHEMISTRY

Connexin32 Mutations Cause Loss of Function in Schwann Cells and Oligodendrocytes Leading to PNS and CNS Myelination Defects

(2009) I. Sargiannidou et al.   JOURNAL OF NEUROSCIENCE

Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy

(2009) N. Cartier et al.   SCIENCE

Applications of Lentiviral Vectors for Biology and Gene Therapy of Neurological Disorders

(2008) Cecilia Lundberg et al.   CURRENT GENE THERAPY

Molecular mechanisms of inherited demyelinating neuropathies

(2008) Steven S. Scherer et al.   GLIA

Cx29 and Cx32, two connexins expressed by myelinating glia, do not interact and are functionally distinct

(2007) Meejin Ahn et al.   JOURNAL OF NEUROSCIENCE RESEARCH