Widespread enzymatic correction of CNS tissues by a single intracerebral injection of therapeutic lentiviral vector in leukodystrophy mouse models
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Title
Widespread enzymatic correction of CNS tissues by a single intracerebral injection of therapeutic lentiviral vector in leukodystrophy mouse models
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 19, Issue 11, Pages 2208-2227
Publisher
Oxford University Press (OUP)
Online
2010-03-05
DOI
10.1093/hmg/ddq099
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