Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy
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Title
Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 23, Issue 12, Pages 3250-3268
Publisher
Oxford University Press (OUP)
Online
2014-01-25
DOI
10.1093/hmg/ddu034
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