Spinal muscular atrophy: antisense oligonucleotide therapy opens the door to an integrated therapeutic landscape
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Title
Spinal muscular atrophy: antisense oligonucleotide therapy opens the door to an integrated therapeutic landscape
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 26, Issue R2, Pages R151-R159
Publisher
Oxford University Press (OUP)
Online
2017-06-06
DOI
10.1093/hmg/ddx215
References
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