A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse
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Title
A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 21, Issue 7, Pages 1625-1638
Publisher
Oxford University Press (OUP)
Online
2011-12-21
DOI
10.1093/hmg/ddr600
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