Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy
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Title
Systemic peptide-mediated oligonucleotide therapy improves long-term survival in spinal muscular atrophy
Authors
Keywords
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Journal
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Volume 113, Issue 39, Pages 10962-10967
Publisher
Proceedings of the National Academy of Sciences
Online
2016-09-13
DOI
10.1073/pnas.1605731113
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