Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells
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Title
Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells
Authors
Keywords
CRISPR-Cas gene editing, hematopoietic stem cells, mobilization, X-linked hyper-IgM syndrome, human hematochimeric mouse model, RNA-based delivery, autologous stem cell transplantation, gene transfer, conditioning-free
Journal
CELL
Volume -, Issue -, Pages -
Publisher
Elsevier BV
Online
2022-05-25
DOI
10.1016/j.cell.2022.04.039
References
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