Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells
出版年份 2022 全文链接
标题
Mobilization-based chemotherapy-free engraftment of gene-edited human hematopoietic stem cells
作者
关键词
CRISPR-Cas gene editing, hematopoietic stem cells, mobilization, X-linked hyper-IgM syndrome, human hematochimeric mouse model, RNA-based delivery, autologous stem cell transplantation, gene transfer, conditioning-free
出版物
CELL
Volume -, Issue -, Pages -
出版商
Elsevier BV
发表日期
2022-05-25
DOI
10.1016/j.cell.2022.04.039
参考文献
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注意:仅列出部分参考文献,下载原文获取全部文献信息。- Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome
- (2021) Valentina Vavassori et al. EMBO Molecular Medicine
- Single-dose MGTA-145/plerixafor leads to efficient mobilization and in vivo transduction of HSCs with thalassemia correction in mice
- (2021) Chang Li et al. Blood Advances
- BAR-Seq clonal tracking of gene-edited cells
- (2021) Samuele Ferrari et al. Nature Protocols
- Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year series
- (2021) Daniele Canarutto et al. Molecular Therapy-Methods & Clinical Development
- Mobilization‐based transplantation of young‐donor hematopoietic stem cells extends lifespan in mice
- (2020) Michael J. Guderyon et al. AGING CELL
- The promise and challenge of therapeutic genome editing
- (2020) Jennifer A. Doudna NATURE
- CXCR4 expression in the bone marrow microenvironment is required for hematopoietic stem and progenitor cell maintenance and early hematopoietic regeneration after myeloablation
- (2020) Pratibha Singh et al. STEM CELLS
- Efficient gene editing of human long-term hematopoietic stem cells validated by clonal tracking
- (2020) Samuele Ferrari et al. NATURE BIOTECHNOLOGY
- Stem cell homing: From physiology to therapeutics
- (2020) Jane L. Liesveld et al. STEM CELLS
- Chimerism in the Realm of Hematopoietic Stem Cell Transplantation for Non-malignant Disorders—A Perspective
- (2020) Clare Zimmerman et al. Frontiers in Immunology
- History of hematopoietic cell transplantation: challenges and progress
- (2020) Noa Granot et al. HAEMATOLOGICA
- Gene therapy using haematopoietic stem and progenitor cells
- (2020) Giuliana Ferrari et al. NATURE REVIEWS GENETICS
- Anti-human CD117 antibody-mediated bone marrow niche clearance in non-human primates and humanized NSG mice
- (2019) Hye-Sook Kwon et al. BLOOD
- Genetic engineering of hematopoiesis: current stage of clinical translation and future perspectives
- (2019) Luigi Naldini EMBO Molecular Medicine
- Hematopoietic stem cell transplantation for CD40 ligand deficiency: results from an EBMT/ESID-IEWP-SCETIDE-PIDTC Study
- (2019) Francesca Ferrua et al. JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY
- Precise Gene Editing Preserves Hematopoietic Stem Cell Function following Transient p53-Mediated DNA Damage Response
- (2019) Giulia Schiroli et al. Cell Stem Cell
- Cytokine‐induced hematopoietic stem and progenitor cell mobilization: unraveling interactions between stem cells and their niche
- (2019) Evert‐Jan F.M. Kruijf et al. Annals of the New York Academy of Sciences
- Design of in vitro Transcribed mRNA Vectors for Research and Therapy
- (2019) Marina Tusup et al. CHIMIA
- Long-term ex vivo haematopoietic-stem-cell expansion allows nonconditioned transplantation
- (2019) Adam C. Wilkinson et al. NATURE
- Antibody Conditioning Enables MHC-Mismatched Hematopoietic Stem Cell Transplants and Organ Graft Tolerance
- (2019) Benson M. George et al. Cell Stem Cell
- Extensive multilineage analysis in patients with mixed chimerism after allogeneic transplantation for sickle cell disease: insight into hematopoiesis and engraftment thresholds for gene therapy
- (2019) Alessandra Magnani et al. HAEMATOLOGICA
- Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
- (2019) Paula Río et al. NATURE MEDICINE
- Non-toxic HSC Transplantation-Based Macrophage/Microglia-Mediated GDNF Delivery for Parkinson’s Disease
- (2019) Cang Chen et al. Molecular Therapy-Methods & Clinical Development
- A Conditioning Regimen with Plerixafor Is Safe and Improves the Outcome of TCRαβ + and CD19 + Cell-Depleted Stem Cell Transplantation in Patients with Wiskott-Aldrich Syndrome
- (2018) Dmitry Balashov et al. BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION
- Allogeneic hematopoietic cell transplantation; the current renaissance
- (2018) Edward A. Copelan et al. BLOOD REVIEWS
- Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1
- (2017) Giulia Schiroli et al. Science Translational Medicine
- Autologous Stem Cell Mobilization and Collection
- (2016) Yen-Michael S. Hsu et al. HEMATOLOGY-ONCOLOGY CLINICS OF NORTH AMERICA
- Cellular players of hematopoietic stem cell mobilization in the bone marrow niche
- (2016) Joshua Tay et al. INTERNATIONAL JOURNAL OF HEMATOLOGY
- New agents in HSC mobilization
- (2016) Mélanie J. Domingues et al. INTERNATIONAL JOURNAL OF HEMATOLOGY
- Non-genotoxic conditioning for hematopoietic stem cell transplantation using a hematopoietic-cell-specific internalizing immunotoxin
- (2016) Rahul Palchaudhuri et al. NATURE BIOTECHNOLOGY
- Hematopoietic stem cell transplantation in immunocompetent hosts without radiation or chemotherapy
- (2016) Akanksha Chhabra et al. Science Translational Medicine
- Therapeutic targeting and rapid mobilization of endosteal HSC using a small molecule integrin antagonist
- (2016) Benjamin Cao et al. Nature Communications
- Leukemia cell mobilization with G-CSF plus plerixafor during busulfan–fludarabine conditioning for allogeneic stem cell transplantation
- (2015) M Konopleva et al. BONE MARROW TRANSPLANTATION
- Emerging Strategies to Enhance Homing and Engraftment of Hematopoietic Stem Cells
- (2015) Mariusz Z. Ratajczak et al. Stem Cell Reviews and Reports
- Emerging Strategies to Enhance Homing and Engraftment of Hematopoietic Stem Cells
- (2015) Mariusz Z. Ratajczak et al. Stem Cell Reviews and Reports
- Conditioning regimens for hematopoietic cell transplantation: one size does not fit all
- (2014) B. Gyurkocza et al. BLOOD
- G-CSF: From granulopoietic stimulant to bone marrow stem cell mobilizing agent
- (2014) Linda J. Bendall et al. CYTOKINE & GROWTH FACTOR REVIEWS
- The Two Human CXCR4 Isoforms Display Different HIV Receptor Activities: Consequences for the Emergence of X4 Strains
- (2014) Charline Duquenne et al. JOURNAL OF IMMUNOLOGY
- A trial of plerixafor adjunctive therapy in allogeneic hematopoietic cell transplantation with minimal conditioning for severe combined immunodeficiency
- (2014) Christopher C. Dvorak et al. PEDIATRIC TRANSPLANTATION
- Hematopoietic stem cell mobilizing agents G-CSF, cyclophosphamide or AMD3100 have distinct mechanisms of action on bone marrow HSC niches and bone formation
- (2012) I G Winkler et al. LEUKEMIA
- Safety and efficacy of healthy volunteer stem cell mobilization with filgrastim G-CSF and mobilized stem cell apheresis: results of a prospective longitudinal 5-year follow-up study
- (2012) M. M. Mueller et al. VOX SANGUINIS
- A point mutation (G574A) in the chemokine receptor CXCR4 detected in human cancer cells enhances migration
- (2010) Caterina Ieranò et al. CELL CYCLE
- Update on clinical experience with AMD3100, an SDF-1/CXCL12–CXCR4 inhibitor, in mobilization of hematopoietic stem and progenitor cells
- (2010) Iskra Pusic et al. CURRENT OPINION IN HEMATOLOGY
- Quantitatively different red cell/nucleated cell chimerism in patients with long-term, persistent hematopoietic mixed chimerism after bone marrow transplantation for thalassemia major or sickle cell disease
- (2010) M. Andreani et al. HAEMATOLOGICA
- AMD3100 is a potent antagonist at CXCR4R334X, a hyperfunctional mutant chemokine receptor and cause of WHIM syndrome
- (2010) David H. McDermott et al. JOURNAL OF CELLULAR AND MOLECULAR MEDICINE
- Mechanisms of G-CSF-mediated hematopoietic stem and progenitor mobilization
- (2010) A M Greenbaum et al. LEUKEMIA
- FDA Review Summary: Mozobil in Combination with Granulocyte Colony-Stimulating Factor to Mobilize Hematopoietic Stem Cells to the Peripheral Blood for Collection and Subsequent Autologous Transplantation
- (2010) Michael Brave et al. ONCOLOGY
- Hematopoietic stem cell: self-renewal versus differentiation
- (2010) Jun Seita et al. Wiley Interdisciplinary Reviews-Systems Biology and Medicine
- BIO5192, a small molecule inhibitor of VLA-4, mobilizes hematopoietic stem and progenitor cells
- (2009) P. Ramirez et al. BLOOD
- Adverse events among 2408 unrelated donors of peripheral blood stem cells: results of a prospective trial from the National Marrow Donor Program
- (2009) M. A. Pulsipher et al. BLOOD
- CD47 Is Upregulated on Circulating Hematopoietic Stem Cells and Leukemia Cells to Avoid Phagocytosis
- (2009) Siddhartha Jaiswal et al. CELL
- Niche recycling through division-independent egress of hematopoietic stem cells
- (2009) Deepta Bhattacharya et al. JOURNAL OF EXPERIMENTAL MEDICINE
- Enrichment of hematopoietic stem cells with SLAM and LSK markers for the detection of hematopoietic stem cell function in normal and Trp53 null mice
- (2008) Jichun Chen et al. EXPERIMENTAL HEMATOLOGY
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