Recent progress and considerations for AAV gene therapies targeting the central nervous system
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Title
Recent progress and considerations for AAV gene therapies targeting the central nervous system
Authors
Keywords
Central nervous system, Adeno-associated virus, AAV9, Gene therapy, Clinical trial, Neutralizing antibody, Cellular immunity
Journal
Journal of Neurodevelopmental Disorders
Volume 10, Issue 1, Pages -
Publisher
Springer Nature
Online
2018-05-18
DOI
10.1186/s11689-018-9234-0
References
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