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Title
Therapeutic approaches for spinal muscular atrophy (SMA)
Authors
Keywords
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Journal
GENE THERAPY
Volume 24, Issue 9, Pages 514-519
Publisher
Springer Nature
Online
2017-05-31
DOI
10.1038/gt.2017.45
References
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Related references
Note: Only part of the references are listed.- Small Molecules in Development for the Treatment of Spinal Muscular Atrophy
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