CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy
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Title
CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy
Authors
Keywords
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Journal
JOURNAL OF CLINICAL INVESTIGATION
Volume 120, Issue 4, Pages 1253-1264
Publisher
American Society for Clinical Investigation
Online
2010-03-17
DOI
10.1172/jci41615
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