Peptide-guided lipid nanoparticles deliver mRNA to the neural retina of rodents and nonhuman primates
Published 2023 View Full Article
- Home
- Publications
- Publication Search
- Publication Details
Title
Peptide-guided lipid nanoparticles deliver mRNA to the neural retina of rodents and nonhuman primates
Authors
Keywords
-
Journal
Science Advances
Volume 9, Issue 2, Pages -
Publisher
American Association for the Advancement of Science (AAAS)
Online
2023-01-12
DOI
10.1126/sciadv.add4623
References
Ask authors/readers for more resources
Related references
Note: Only part of the references are listed.- A Comprehensive Atlas of Immunological Differences Between Humans, Mice, and Non-Human Primates
- (2022) Zachary B. Bjornson-Hooper et al. Frontiers in Immunology
- Efficacy and Safety of Intravitreal Gene Therapy for Leber Hereditary Optic Neuropathy Treated within 6 Months of Disease Onset
- (2021) Nancy J. Newman et al. OPHTHALMOLOGY
- Inherited retinal diseases: Therapeutics, clinical trials and end‐points ‐ A review
- (2021) Michalis Georgiou et al. CLINICAL AND EXPERIMENTAL OPHTHALMOLOGY
- In vivo CRISPR base editing of PCSK9 durably lowers cholesterol in primates
- (2021) Kiran Musunuru et al. NATURE
- Partial recovery of visual function in a blind patient after optogenetic therapy
- (2021) José-Alain Sahel et al. NATURE MEDICINE
- The current landscape of nucleic acid therapeutics
- (2021) Jayesh A. Kulkarni et al. Nature Nanotechnology
- mRNA vaccines for infectious diseases: principles, delivery and clinical translation
- (2021) Namit Chaudhary et al. NATURE REVIEWS DRUG DISCOVERY
- CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis
- (2021) Julian D. Gillmore et al. NEW ENGLAND JOURNAL OF MEDICINE
- Lipid nanoparticles for mRNA delivery
- (2021) Xucheng Hou et al. Nature Reviews Materials
- Peptide-Enabled Targeted Delivery Systems for Therapeutic Applications
- (2021) Mingpeng Liu et al. Frontiers in Bioengineering and Biotechnology
- Gene Therapy in Inherited Retinal Diseases: An Update on Current State of the Art
- (2021) Alessia Amato et al. Frontiers in Medicine
- CRISPR treatment inserted directly into the body for first time
- (2020) Heidi Ledford NATURE
- CRISPR-Cas9 DNA Base-Editing and Prime-Editing
- (2020) Ariel Kantor et al. INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
- Immune responses to retinal gene therapy using adeno-associated viral vectors – Implications for treatment success and safety
- (2020) Kirsten Bucher et al. PROGRESS IN RETINAL AND EYE RESEARCH
- Efficacy and Safety of the mRNA-1273 SARS-CoV-2 Vaccine
- (2020) Lindsey R. Baden et al. NEW ENGLAND JOURNAL OF MEDICINE
- Safety and Efficacy of the BNT162b2 mRNA Covid-19 Vaccine
- (2020) Fernando P. Polack et al. NEW ENGLAND JOURNAL OF MEDICINE
- Peptide-Based Drug-Delivery Systems in Biotechnological Applications: Recent Advances and Perspectives
- (2019) Diego Tesauro et al. MOLECULES
- Tumor Targeting by Peptide-Decorated Gold Nanoparticles
- (2019) Barbara Albertini et al. MOLECULAR PHARMACEUTICS
- Four technologies that could transform the treatment of blindness
- (2019) Simon Makin NATURE
- Lipid nanoparticles for delivery of messenger RNA to the back of the eye
- (2019) Siddharth Patel et al. JOURNAL OF CONTROLLED RELEASE
- Molecular Therapies for Inherited Retinal Diseases—Current Standing, Opportunities and Challenges
- (2019) Irene Vázquez-Domínguez et al. Genes
- Progress in treating inherited retinal diseases: Early subretinal gene therapy clinical trials and candidates for future initiatives
- (2019) Alexandra V. Garafalo et al. PROGRESS IN RETINAL AND EYE RESEARCH
- A Novel Amino Lipid Series for mRNA Delivery: Improved Endosomal Escape and Sustained Pharmacology and Safety in Non-human Primates
- (2018) Staci Sabnis et al. MOLECULAR THERAPY
- Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis
- (2018) David Adams et al. NEW ENGLAND JOURNAL OF MEDICINE
- Müller glia and phagocytosis of cell debris in retinal tissue
- (2017) Ruth Bejarano-Escobar et al. JOURNAL OF ANATOMY
- microRNA expression in the neural retina: Focus on Müller glia
- (2017) Heberto Quintero et al. JOURNAL OF NEUROSCIENCE RESEARCH
- Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65 -mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial
- (2017) Stephen Russell et al. LANCET
- Lipid Nanoparticle Systems for Enabling Gene Therapies
- (2017) Pieter R. Cullis et al. MOLECULAR THERAPY
- Biology and therapy of inherited retinal degenerative disease: insights from mouse models
- (2015) Shobi Veleri et al. Disease Models & Mechanisms
- Understanding photoreceptor outer segment phagocytosis: Use and utility of RPE cells in culture
- (2014) Francesca Mazzoni et al. EXPERIMENTAL EYE RESEARCH
- New functions of Müller cells
- (2013) Andreas Reichenbach et al. GLIA
Find Funding. Review Successful Grants.
Explore over 25,000 new funding opportunities and over 6,000,000 successful grants.
ExploreFind the ideal target journal for your manuscript
Explore over 38,000 international journals covering a vast array of academic fields.
Search