Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy
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Title
Assessment of systemic AAV-microdystrophin gene therapy in the GRMD model of Duchenne muscular dystrophy
Authors
Keywords
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Journal
Science Translational Medicine
Volume 15, Issue 677, Pages -
Publisher
American Association for the Advancement of Science (AAAS)
Online
2023-01-05
DOI
10.1126/scitranslmed.abo1815
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