A Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular Dystrophy

Title
A Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular Dystrophy
Authors
Keywords
AAV, DMD, micro-dystrophin, mdx, DBA/2J, nNOS, cardiomyopathy, systemic gene therapy, Duchenne muscular dystrophy, adeno-associated virus
Journal
Publisher
Elsevier BV
Online
2017-07-28
DOI
10.1016/j.omtm.2017.06.006

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