Current and emerging therapies for Duchenne muscular dystrophy and spinal muscular atrophy
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Title
Current and emerging therapies for Duchenne muscular dystrophy and spinal muscular atrophy
Authors
Keywords
Duchenne muscular dystrophy, Spinal muscular atrophy, SMN1 gene, Dystrophin protein, Autosomal-recessive disorder
Journal
PHARMACOLOGY & THERAPEUTICS
Volume 220, Issue -, Pages 107719
Publisher
Elsevier BV
Online
2020-10-30
DOI
10.1016/j.pharmthera.2020.107719
References
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