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Title
Gene therapy for ALS: A review
Authors
Keywords
ALS, amyotrophic lateral sclerosis, gene therapy, AAV, ASO, RNAi, CRISPR, gene delivery, clinical trial
Journal
MOLECULAR THERAPY
Volume -, Issue -, Pages -
Publisher
Elsevier BV
Online
2021-04-09
DOI
10.1016/j.ymthe.2021.04.008
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