Cas9 gene therapy for Angelman syndrome traps Ube3a-ATS long non-coding RNA
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Title
Cas9 gene therapy for Angelman syndrome traps Ube3a-ATS long non-coding RNA
Authors
Keywords
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Journal
NATURE
Volume -, Issue -, Pages -
Publisher
Springer Science and Business Media LLC
Online
2020-10-22
DOI
10.1038/s41586-020-2835-2
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