标题
Current Clinical Applications of In Vivo Gene Therapy with AAVs
作者
关键词
-
出版物
MOLECULAR THERAPY
Volume -, Issue -, Pages -
出版商
Elsevier BV
发表日期
2020-12-10
DOI
10.1016/j.ymthe.2020.12.007
参考文献
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- Restoration of Cone Vision in the CNGA3−/− Mouse Model of Congenital Complete Lack of Cone Photoreceptor Function
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- Preclinical Safety Evaluation of AAV2-sFLT01— A Gene Therapy for Age-related Macular Degeneration
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