Long-Term Safety and Efficacy of Factor IX Gene Therapy in Hemophilia B

Randomized, multicenter trial comparing tacrolimus plus mycophenolate mofetil to tacrolimus plus steroids in hepatitis C virus-positive recipients of living donor liver transplantation

(2013) Yasutsugu Takada et al.   LIVER TRANSPLANTATION

The hope and reality of long-acting hemophilia products

(2012) Steven W. Pipe   AMERICAN JOURNAL OF HEMATOLOGY

Systemic Errors in Quantitative Polymerase Chain Reaction Titration of Self-Complementary Adeno-Associated Viral Vectors and Improved Alternative Methods

(2012) Paolo Fagone et al.   Human Gene Therapy Methods

Good Manufacturing Practice Production of Self-Complementary Serotype 8 Adeno-Associated Viral Vector for a Hemophilia B Clinical Trial

(2011) James A. Allay et al.   HUMAN GENE THERAPY

Long-term Safety and Efficacy Following Systemic Administration of a Self-complementary AAV Vector Encoding Human FIX Pseudotyped With Serotype 5 and 8 Capsid Proteins

(2011) Amit C Nathwani et al.   MOLECULAR THERAPY

Adenovirus-Associated Virus Vector–Mediated Gene Transfer in Hemophilia B

(2011) Amit C. Nathwani et al.   NEW ENGLAND JOURNAL OF MEDICINE

Analysis of low frequency bleeding data: the association of joint bleeds according to baseline FVIII activity levels

(2010) I. E. M. DEN UIJL et al.   HAEMOPHILIA

Walk a mile in the moccasins of people with haemophilia

(2008) K. P. PONDER et al.   HAEMOPHILIA