Novel AAV44.9-Based Vectors Display Exceptional Characteristics for Retinal Gene Therapy

标题
Novel AAV44.9-Based Vectors Display Exceptional Characteristics for Retinal Gene Therapy
作者
关键词
AAV, subretinal injection, AAV44.9(E531D), retina, gene therapy, inherited retinal disease, rational design, macaque, lateral spread
出版物
MOLECULAR THERAPY
Volume -, Issue -, Pages -
出版商
Elsevier BV
发表日期
2020-04-11
DOI
10.1016/j.ymthe.2020.04.002

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