Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant

标题
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant
作者
关键词
-
出版物
NEW ENGLAND JOURNAL OF MEDICINE
Volume 377, Issue 23, Pages 2215-2227
出版商
New England Journal of Medicine (NEJM/MMS)
发表日期
2017-12-07
DOI
10.1056/nejmoa1708538

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