标题
Use of Customizable Nucleases for Gene Editing and Other Novel Applications
作者
关键词
-
出版物
Genes
Volume 11, Issue 9, Pages 976
出版商
MDPI AG
发表日期
2020-08-24
DOI
10.3390/genes11090976
参考文献
相关参考文献
注意:仅列出部分参考文献,下载原文获取全部文献信息。- Age-Associated B Cells
- (2020) Michael P. Cancro Annual Review of Immunology
- Mitochondrial DNA heteroplasmy in disease and targeted nuclease‐based therapeutic approaches
- (2020) Nadee Nissanka et al. EMBO REPORTS
- CRISPR/Cas9‐mediated genome editing: From basic research to translational medicine
- (2020) Filipe V. Jacinto et al. JOURNAL OF CELLULAR AND MOLECULAR MEDICINE
- Treatment of a Mouse Model of ALS by In Vivo Base Editing
- (2020) Colin K.W. Lim et al. MOLECULAR THERAPY
- The promise and challenge of therapeutic genome editing
- (2020) Jennifer A. Doudna NATURE
- Fast and efficient generation of knock-in human organoids using homology-independent CRISPR–Cas9 precision genome editing
- (2020) Benedetta Artegiani et al. NATURE CELL BIOLOGY
- The ageing epigenome and its rejuvenation
- (2020) Weiqi Zhang et al. NATURE REVIEWS MOLECULAR CELL BIOLOGY
- Toward Guidelines for Research on Human Embryo Models Formed from Stem Cells
- (2020) Insoo Hyun et al. Stem Cell Reports
- CRISPR-Based Synthetic Transcription Factors In Vivo: The Future of Therapeutic Cellular Programming
- (2020) Matthew Pandelakis et al. Cell Systems
- Development of CRISPR as an Antiviral Strategy to Combat SARS-CoV-2 and Influenza
- (2020) Timothy R. Abbott et al. CELL
- CRISPR–Cas12-based detection of SARS-CoV-2
- (2020) James P. Broughton et al. NATURE BIOTECHNOLOGY
- Dual base editor catalyzes both cytosine and adenine base conversions in human cells
- (2020) Xiaohui Zhang et al. NATURE BIOTECHNOLOGY
- A dual-deaminase CRISPR base editor enables concurrent adenine and cytosine editing
- (2020) Julian Grünewald et al. NATURE BIOTECHNOLOGY
- Base editors for simultaneous introduction of C-to-T and A-to-G mutations
- (2020) Rina C. Sakata et al. NATURE BIOTECHNOLOGY
- Determinants of Base Editing Outcomes from Target Library Analysis and Machine Learning
- (2020) Mandana Arbab et al. CELL
- Glycosylase base editors enable C-to-A and C-to-G base changes
- (2020) Dongdong Zhao et al. NATURE BIOTECHNOLOGY
- Exploiting CRISPR Cas9 in Three-Dimensional Stem Cell Cultures to Model Disease
- (2020) Sneha Gopal et al. Frontiers in Bioengineering and Biotechnology
- Diversifying the structure of zinc finger nucleases for high-precision genome editing
- (2019) David E. Paschon et al. Nature Communications
- Identification of preexisting adaptive immunity to Cas9 proteins in humans
- (2019) Carsten T. Charlesworth et al. NATURE MEDICINE
- Development of a CRISPR/Cas9-based therapy for Hutchinson–Gilford progeria syndrome
- (2019) Olaya Santiago-Fernández et al. NATURE MEDICINE
- Single-dose CRISPR–Cas9 therapy extends lifespan of mice with Hutchinson–Gilford progeria syndrome
- (2019) Ergin Beyret et al. NATURE MEDICINE
- The next generation of CRISPR–Cas technologies and applications
- (2019) Adrian Pickar-Oliver et al. NATURE REVIEWS MOLECULAR CELL BIOLOGY
- Rescue of premature aging defects in Cockayne syndrome stem cells by CRISPR/Cas9-mediated gene correction
- (2019) Si Wang et al. Protein & Cell
- Design Approaches for Generating Organ Constructs
- (2019) Yun Xia et al. Cell Stem Cell
- Transposon-encoded CRISPR–Cas systems direct RNA-guided DNA integration
- (2019) Sanne E. Klompe et al. NATURE
- Hijack of CRISPR defences by selfish genes holds clinical promise
- (2019) Fyodor D. Urnov NATURE
- Principles of and strategies for germline gene therapy
- (2019) Don P. Wolf et al. NATURE MEDICINE
- Creation of CRISPR-based germline-genome-engineered mice without ex vivo handling of zygotes by i-GONAD
- (2019) Channabasavaiah B. Gurumurthy et al. Nature Protocols
- Organoids by design
- (2019) Takanori Takebe et al. SCIENCE
- Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction
- (2019) Keiichiro Suzuki et al. CELL RESEARCH
- Generation of Blastocyst-like Structures from Mouse Embryonic and Adult Cell Cultures
- (2019) Ronghui Li et al. CELL
- Search-and-replace genome editing without double-strand breaks or donor DNA
- (2019) Andrew V. Anzalone et al. NATURE
- Dose-dependent activation of gene expression is achieved using CRISPR and small molecules that recruit endogenous chromatin machinery
- (2019) Anna M. Chiarella et al. NATURE BIOTECHNOLOGY
- Transcriptome Engineering with RNA-Targeting Type VI-D CRISPR Effectors
- (2018) Silvana Konermann et al. CELL
- Cas13d Is a Compact RNA-Targeting Type VI CRISPR Effector Positively Modulated by a WYL-Domain-Containing Accessory Protein
- (2018) Winston X. Yan et al. MOLECULAR CELL
- In Situ Gene Therapy via AAV-CRISPR-Cas9-Mediated Targeted Gene Regulation
- (2018) Ana M. Moreno et al. MOLECULAR THERAPY
- CRISPR interference-based specific and efficient gene inactivation in the brain
- (2018) Yi Zheng et al. NATURE NEUROSCIENCE
- In vivo simultaneous transcriptional activation of multiple genes in the brain using CRISPR–dCas9-activator transgenic mice
- (2018) Haibo Zhou et al. NATURE NEUROSCIENCE
- Engineering altered protein–DNA recognition specificity
- (2018) Adam J Bogdanove et al. NUCLEIC ACIDS RESEARCH
- Field-deployable viral diagnostics using CRISPR-Cas13
- (2018) Cameron Myhrvold et al. SCIENCE
- CRISPR-Cas12a target binding unleashes indiscriminate single-stranded DNase activity
- (2018) Janice S. Chen et al. SCIENCE
- Multiplexed and portable nucleic acid detection platform with Cas13, Cas12a, and Csm6
- (2018) Jonathan S. Gootenberg et al. SCIENCE
- Mitochondrial Genome Engineering: The Revolution May Not Be CRISPR-Ized
- (2018) Payam A. Gammage et al. TRENDS IN GENETICS
- In vivo base editing of post-mitotic sensory cells
- (2018) Wei-Hsi Yeh et al. Nature Communications
- The CRISPR tool kit for genome editing and beyond
- (2018) Mazhar Adli Nature Communications
- RNA-guided transcriptional silencing in vivo with S. aureus CRISPR-Cas9 repressors
- (2018) Pratiksha I. Thakore et al. Nature Communications
- Age-related differences in humoral and cellular immune responses after primary immunisation: indications for stratified vaccination schedules
- (2018) Angelika Wagner et al. Scientific Reports
- Aging and the rise of somatic cancer-associated mutations in normal tissues
- (2018) Rosa Ana Risques et al. PLoS Genetics
- Correction of the Marfan Syndrome Pathogenic FBN1 Mutation by Base Editing in Human Cells and Heterozygous Embryos
- (2018) Yanting Zeng et al. MOLECULAR THERAPY
- MitoTALEN reduces mutant mtDNA load and restores tRNAAla levels in a mouse model of heteroplasmic mtDNA mutation
- (2018) Sandra R. Bacman et al. NATURE MEDICINE
- Genome editing in mitochondria corrects a pathogenic mtDNA mutation in vivo
- (2018) Payam A. Gammage et al. NATURE MEDICINE
- CRISPR-Cas guides the future of genetic engineering
- (2018) Gavin J. Knott et al. SCIENCE
- Cas9 immunity creates challenges for CRISPR gene editing therapies
- (2018) Julie M. Crudele et al. Nature Communications
- Debate ethics of embryo models from stem cells
- (2018) Nicolas Rivron et al. NATURE
- Multiplexed orthogonal genome editing and transcriptional activation by Cas12a
- (2018) Marco Breinig et al. NATURE METHODS
- Base editing: precision chemistry on the genome and transcriptome of living cells
- (2018) Holly A. Rees et al. NATURE REVIEWS GENETICS
- CRISPR-mediated activation of a promoter or enhancer rescues obesity caused by haploinsufficiency
- (2018) Navneet Matharu et al. SCIENCE
- In vivo genome editing via the HITI method as a tool for gene therapy
- (2017) Keiichiro Suzuki et al. JOURNAL OF HUMAN GENETICS
- CRISPR/Cas9-mediated gene editing in human zygotes using Cas9 protein
- (2017) Lichun Tang et al. MOLECULAR GENETICS AND GENOMICS
- Programmable base editing of A•T to G•C in genomic DNA without DNA cleavage
- (2017) Nicole M. Gaudelli et al. NATURE
- Correction of a pathogenic gene mutation in human embryos
- (2017) Hong Ma et al. NATURE
- Genome editing reveals a role for OCT4 in human embryogenesis
- (2017) Norah M. E. Fogarty et al. NATURE
- Am I ready for CRISPR? A user's guide to genetic screens
- (2017) John G. Doench NATURE REVIEWS GENETICS
- Recruitment of CRISPR-Cas systems by Tn7-like transposons
- (2017) Joseph E. Peters et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- RNA editing with CRISPR-Cas13
- (2017) David B. T. Cox et al. SCIENCE
- Nucleic acid detection with CRISPR-Cas13a/C2c2
- (2017) Jonathan S. Gootenberg et al. SCIENCE
- Assembly of embryonic and extraembryonic stem cells to mimic embryogenesis in vitro
- (2017) Sarah Ellys Harrison et al. SCIENCE
- CRISPR/Cas9-mediated PD-1 disruption enhances anti-tumor efficacy of human chimeric antigen receptor T cells
- (2017) Levi J. Rupp et al. Scientific Reports
- Introducing precise genetic modifications into human 3PN embryos by CRISPR/Cas-mediated genome editing
- (2016) Xiangjin Kang et al. JOURNAL OF ASSISTED REPRODUCTION AND GENETICS
- In vivo genome editing via CRISPR/Cas9 mediated homology-independent targeted integration
- (2016) Keiichiro Suzuki et al. NATURE
- Self-organization of the in vitro attached human embryo
- (2016) Alessia Deglincerti et al. NATURE
- Programmable editing of a target base in genomic DNA without double-stranded DNA cleavage
- (2016) Alexis C. Komor et al. NATURE
- CRISPR knockout screening outperforms shRNA and CRISPRi in identifying essential genes
- (2016) Bastiaan Evers et al. NATURE BIOTECHNOLOGY
- A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
- (2016) Yang Yang et al. NATURE BIOTECHNOLOGY
- Self-organization of the human embryo in the absence of maternal tissues
- (2016) Marta N. Shahbazi et al. NATURE CELL BIOLOGY
- A multifunctional AAV–CRISPR–Cas9 and its host response
- (2016) Wei Leong Chew et al. NATURE METHODS
- Editing the epigenome: technologies for programmable transcription and epigenetic modulation
- (2016) Pratiksha I Thakore et al. NATURE METHODS
- Targeted nucleotide editing using hybrid prokaryotic and vertebrate adaptive immune systems
- (2016) K. Nishida et al. SCIENCE
- C2c2 is a single-component programmable RNA-guided RNA-targeting CRISPR effector
- (2016) Omar O. Abudayyeh et al. SCIENCE
- Anti-Aging Strategies Based on Cellular Reprogramming
- (2016) Alejandro Ocampo et al. TRENDS IN MOLECULAR MEDICINE
- The CRISPR-Cas immune system: Biology, mechanisms and applications
- (2015) Devashish Rath et al. BIOCHIMIE
- Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells
- (2015) M. D. Hoban et al. BLOOD
- Selective Elimination of Mitochondrial Mutations in the Germline by Genome Editing
- (2015) Pradeep Reddy et al. CELL
- Genome-scale transcriptional activation by an engineered CRISPR-Cas9 complex
- (2015) Silvana Konermann et al. NATURE
- In vivo genome editing using Staphylococcus aureus Cas9
- (2015) F. Ann Ran et al. NATURE
- Highly efficient Cas9-mediated transcriptional programming
- (2015) Alejandro Chavez et al. NATURE METHODS
- Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy
- (2015) C. Long et al. SCIENCE
- In vivo gene editing in dystrophic mouse muscle and muscle stem cells
- (2015) M. Tabebordbar et al. SCIENCE
- In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
- (2015) C. E. Nelson et al. SCIENCE
- Use of the CRISPR/Cas9 system as an intracellular defense against HIV-1 infection in human cells
- (2015) Hsin-Kai Liao et al. Nature Communications
- CRISPR/Cas9-mediated gene editing in human tripronuclear zygotes
- (2015) Puping Liang et al. Protein & Cell
- Efficient Mitochondrial Genome Editing by CRISPR/Cas9
- (2015) Areum Jo et al. Biomed Research International
- Development and Applications of CRISPR-Cas9 for Genome Engineering
- (2014) Patrick D. Hsu et al. CELL
- Mitochondrially targeted ZFNs for selective degradation of pathogenic mitochondrial genomes bearing large-scale deletions or point mutations
- (2014) P. A. Gammage et al. EMBO Molecular Medicine
- Programmable RNA recognition and cleavage by CRISPR/Cas9
- (2014) Mitchell R. O’Connell et al. NATURE
- RNA-directed gene editing specifically eradicates latent and prevents new HIV-1 infection
- (2014) W. Hu et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Genome Engineering at the Dawn of the Golden Age
- (2013) David J. Segal et al. Annual Review of Genomics and Human Genetics
- One-Step Generation of Mice Carrying Mutations in Multiple Genes by CRISPR/Cas-Mediated Genome Engineering
- (2013) Haoyi Wang et al. CELL
- The Hallmarks of Aging
- (2013) Carlos López-Otín et al. CELL
- Double Nicking by RNA-Guided CRISPR Cas9 for Enhanced Genome Editing Specificity
- (2013) F. Ann Ran et al. CELL
- DNA targeting specificity of RNA-guided Cas9 nucleases
- (2013) Patrick D Hsu et al. NATURE BIOTECHNOLOGY
- Targeted genome engineering in human cells with the Cas9 RNA-guided endonuclease
- (2013) Seung Woo Cho et al. NATURE BIOTECHNOLOGY
- High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells
- (2013) Yanfang Fu et al. NATURE BIOTECHNOLOGY
- Specific elimination of mutant mitochondrial genomes in patient-derived cells by mitoTALENs
- (2013) Sandra R Bacman et al. NATURE MEDICINE
- Live visualization of chromatin dynamics with fluorescent TALEs
- (2013) Yusuke Miyanari et al. NATURE STRUCTURAL & MOLECULAR BIOLOGY
- Chromosomal deletions and inversions mediated by TALENs and CRISPR/Cas in zebrafish
- (2013) An Xiao et al. NUCLEIC ACIDS RESEARCH
- Zinc-finger-nucleases mediate specific and efficient excision of HIV-1 proviral DNA from infected and latently infected human T cells
- (2013) Xiying Qu et al. NUCLEIC ACIDS RESEARCH
- RNA-Guided Human Genome Engineering via Cas9
- (2013) P. Mali et al. SCIENCE
- Genome-Scale CRISPR-Cas9 Knockout Screening in Human Cells
- (2013) Ophir Shalem et al. SCIENCE
- Genetic Screens in Human Cells Using the CRISPR-Cas9 System
- (2013) Tim Wang et al. SCIENCE
- Multiplex Genome Engineering Using CRISPR/Cas Systems
- (2013) L. Cong et al. SCIENCE
- Harnessing the CRISPR/Cas9 system to disrupt latent HIV-1 provirus
- (2013) Hirotaka Ebina et al. Scientific Reports
- RNA-programmed genome editing in human cells
- (2013) Martin Jinek et al. eLife
- Advances in targeted genome editing
- (2012) Pablo Perez-Pinera et al. CURRENT OPINION IN CHEMICAL BIOLOGY
- In vivo genome editing using a high-efficiency TALEN system
- (2012) Victoria M. Bedell et al. NATURE
- TALENs: a widely applicable technology for targeted genome editing
- (2012) J. Keith Joung et al. NATURE REVIEWS MOLECULAR CELL BIOLOGY
- Highly Efficient and Specific Genome Editing in Silkworm Using Custom TALENs
- (2012) Sanyuan Ma et al. PLoS One
- Efficient TALEN-mediated gene knockout in livestock
- (2012) D. F. Carlson et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity
- (2012) M. Jinek et al. SCIENCE
- Meganucleases and Other Tools for Targeted Genome Engineering: Perspectives and Challenges for Gene Therapy
- (2011) George Silva et al. CURRENT GENE THERAPY
- Genome Engineering With Zinc-Finger Nucleases
- (2011) Dana Carroll GENETICS
- In Situ Genetic Correction of the Sickle Cell Anemia Mutation in Human Induced Pluripotent Stem Cells Using Engineered Zinc Finger Nucleases
- (2011) Vittorio Sebastiano et al. STEM CELLS
- XanthomonasAvrBs3 Family-Type III Effectors: Discovery and Function
- (2010) Jens Boch et al. Annual Review of Phytopathology
- Targeted integration in rat and mouse embryos with zinc-finger nucleases
- (2010) Xiaoxia Cui et al. NATURE BIOTECHNOLOGY
- Genome editing with engineered zinc finger nucleases
- (2010) Fyodor D. Urnov et al. NATURE REVIEWS GENETICS
- Gene targeting by homologous recombination in mouse zygotes mediated by zinc-finger nucleases
- (2010) M. Meyer et al. PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
- Knockout Rats via Embryo Microinjection of Zinc-Finger Nucleases
- (2009) Aron M. Geurts et al. SCIENCE
- Zinc-finger Nucleases: The Next Generation Emerges
- (2008) Toni Cathomen et al. MOLECULAR THERAPY
- Establishment of HIV-1 resistance in CD4+ T cells by genome editing using zinc-finger nucleases
- (2008) Elena E Perez et al. NATURE BIOTECHNOLOGY
- Development of a single-chain, quasi-dimeric zinc-finger nuclease for the selective degradation of mutated human mitochondrial DNA
- (2008) Michal Minczuk et al. NUCLEIC ACIDS RESEARCH
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