Safety and potential efficacy of gemfibrozil as a supportive treatment for children with late infantile neuronal ceroid lipofuscinosis and other lipid storage disorders
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Title
Safety and potential efficacy of gemfibrozil as a supportive treatment for children with late infantile neuronal ceroid lipofuscinosis and other lipid storage disorders
Authors
Keywords
Batten disease, NCL, Gemfibrozil, Lipofuscinosis, Central nervous system, Lysosome biogenesis, TPP1, Lopid, CLN2, Children
Journal
Orphanet Journal of Rare Diseases
Volume 12, Issue 1, Pages -
Publisher
Springer Nature
Online
2017-06-17
DOI
10.1186/s13023-017-0663-8
References
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Related references
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