Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl–protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis

Title
Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl–protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis
Authors
Keywords
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Journal
MOLECULAR GENETICS AND METABOLISM
Volume 107, Issue 1-2, Pages 213-221
Publisher
Elsevier BV
Online
2012-05-23
DOI
10.1016/j.ymgme.2012.05.009

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