Knockdown and replacement therapy mediated by artificial mirtrons in spinocerebellar ataxia 7
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Title
Knockdown and replacement therapy mediated by artificial mirtrons in spinocerebellar ataxia 7
Authors
Keywords
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Journal
NUCLEIC ACIDS RESEARCH
Volume 45, Issue 13, Pages 7870-7885
Publisher
Oxford University Press (OUP)
Online
2017-05-27
DOI
10.1093/nar/gkx483
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