Cas9/sgRNA selective targeting of the P23H Rhodopsin mutant allele for treating retinitis pigmentosa by intravitreal AAV9.PHP.B-based delivery
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Title
Cas9/sgRNA selective targeting of the P23H Rhodopsin mutant allele for treating retinitis pigmentosa by intravitreal AAV9.PHP.B-based delivery
Authors
Keywords
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Journal
HUMAN MOLECULAR GENETICS
Volume 27, Issue 5, Pages 761-779
Publisher
Oxford University Press (OUP)
Online
2017-12-21
DOI
10.1093/hmg/ddx438
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