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Title
Nusinersen for the treatment of spinal muscular atrophy
Authors
Keywords
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Journal
Expert Review of Neurotherapeutics
Volume 17, Issue 10, Pages 955-962
Publisher
Informa UK Limited
Online
2017-09-08
DOI
10.1080/14737175.2017.1364159
References
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- Validation of the Childrenʼs Hospital of Philadelphia Infant Test of Neuromuscular Disorders (CHOP INTEND)
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