Revised upper limb module for spinal muscular atrophy: Development of a new module

Spinal muscular atrophy functional composite score: A functional measure in spinal muscular atrophy

(2015) Jacqueline Montes et al.   MUSCLE & NERVE

Upper limb module in non-ambulant patients with spinal muscular atrophy: 12 month changes

(2015) Serena Sivo et al.   NEUROMUSCULAR DISORDERS

209th ENMC International Workshop: Outcome Measures and Clinical Trial Readiness in Spinal Muscular Atrophy 7–9 November 2014, Heemskerk, The Netherlands

(2015) Richard Finkel et al.   NEUROMUSCULAR DISORDERS

Development of the Performance of the Upper Limb module for Duchenne muscular dystrophy

(2013) Anna Mayhew et al.   DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY

Rasch analysis of clinical outcome measures in spinal muscular atrophy

(2013) Stefan J. Cano et al.   MUSCLE & NERVE

SMA-EUROPE workshop report: opportunities and challenges in developing clinical trials for spinal muscular atrophy in Europe

(2013) Nathalie Kayadjanian et al.   Orphanet Journal of Rare Diseases

A critical review of functional assessment tools for upper limbs in Duchenne muscular dystrophy

(2012) ELENA S MAZZONE et al.   DEVELOPMENTAL MEDICINE AND CHILD NEUROLOGY

Assessing upper limb function in nonambulant SMA patients: Development of a new module

(2011) Elena Mazzone et al.   NEUROMUSCULAR DISORDERS

Choosing the right clinical outcome measure: From the patient to the statistician and back

(2010) Eugenio Mercuri et al.   NEUROMUSCULAR DISORDERS

The Cervical Dystonia Impact Profile (CDIP-58): Can a Rasch developed patient reported outcome measure satisfy traditional psychometric criteria?

(2008) Stefan J Cano et al.   Health and Quality of Life Outcomes

Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; Report of three expert workshops: TREAT-NMD/ENMC Workshop on outcome measures, 12th–13th May 2007, Naarden, The Netherlands; TREAT-NMD Workshop on outcome measures in experimental trials for DMD, 30th June–1st July 2007, Naarden, The Netherlands; Conjoint Institute of Myology TREAT-NMD Meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France

(2008) E. Mercuri et al.   NEUROMUSCULAR DISORDERS