Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis
Published 2016 View Full Article
- Home
- Publications
- Publication Search
- Publication Details
Title
Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis
Authors
Keywords
-
Journal
THORAX
Volume 72, Issue 2, Pages 137-147
Publisher
BMJ
Online
2016-11-17
DOI
10.1136/thoraxjnl-2016-208406
References
Ask authors/readers for more resources
Related references
Note: Only part of the references are listed.- Outcomes Following Gene Therapy in Patients With Severe Wiskott-Aldrich Syndrome
- (2015) Salima Hacein-Bey Abina et al. JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION
- Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial
- (2015) Eric W F W Alton et al. Lancet Respiratory Medicine
- Translational Data from Adeno-Associated Virus-Mediated Gene Therapy of Hemophilia B in Dogs
- (2015) Timothy C. Nichols et al. Human Gene Therapy Clinical Development
- Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy
- (2014) A. Lattanzi et al. HUMAN MOLECULAR GENETICS
- Long-term safety and tolerability of ProSavin, a lentiviral vector-based gene therapy for Parkinson's disease: a dose escalation, open-label, phase 1/2 trial
- (2014) Stéphane Palfi et al. LANCET
- Gene therapy of primary T cell immunodeficiencies
- (2013) Alain Fischer et al. GENE
- Current progress on gene therapy for primary immunodeficiencies
- (2013) L Zhang et al. GENE THERAPY
- A functional CFTR assay using primary cystic fibrosis intestinal organoids
- (2013) Johanna F Dekkers et al. NATURE MEDICINE
- Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
- (2013) A. Aiuti et al. SCIENCE
- Lentiviral Hematopoietic Stem Cell Gene Therapy Benefits Metachromatic Leukodystrophy
- (2013) A. Biffi et al. SCIENCE
- Assessment of F/HN-Pseudotyped Lentivirus as a Clinically Relevant Vector for Lung Gene Therapy
- (2012) Uta Griesenbach et al. AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE
- Lentiviral Vector Gene Transfer to Porcine Airways
- (2012) Patrick L Sinn et al. Molecular Therapy-Nucleic Acids
- Lentiviral Vector Integration Profiles Differ in Rodent Postmitotic Tissues
- (2011) Cynthia C Bartholomae et al. MOLECULAR THERAPY
- Validation of recombinant Sendai virus in a non-natural host model
- (2010) U Griesenbach et al. GENE THERAPY
- Toward Gene Therapy for Cystic Fibrosis Using a Lentivirus Pseudotyped With Sendai Virus Envelopes
- (2010) Katsuyuki Mitomo et al. MOLECULAR THERAPY
- A Ubiquitous Chromatin Opening Element (UCOE) Confers Resistance to DNA Methylation–mediated Silencing of Lentiviral Vectors
- (2010) Fang Zhang et al. MOLECULAR THERAPY
- Stem-Cell Gene Therapy for the Wiskott–Aldrich Syndrome
- (2010) Kaan Boztug et al. NEW ENGLAND JOURNAL OF MEDICINE
- Ion transport across CF and normal murine olfactory and ciliated epithelium
- (2009) B. R. Grubb et al. AMERICAN JOURNAL OF PHYSIOLOGY-CELL PHYSIOLOGY
- Limitations of the Murine Nose in the Development of Nonviral Airway Gene Transfer
- (2009) Uta Griesenbach et al. AMERICAN JOURNAL OF RESPIRATORY CELL AND MOLECULAR BIOLOGY
- Development of inducible EIAV-based lentiviral vector packaging and producer cell lines
- (2009) H J Stewart et al. GENE THERAPY
- Amelioration of emphysema in mice through lentiviral transduction of long-lived pulmonary alveolar macrophages
- (2009) Andrew A. Wilson et al. JOURNAL OF CLINICAL INVESTIGATION
- Validation of Nasal Potential Difference Measurements in Gut-Corrected CF Knockout Mice
- (2008) Uta Griesenbach et al. AMERICAN JOURNAL OF RESPIRATORY CELL AND MOLECULAR BIOLOGY
- Lentivirus Vector Can Be Readministered to Nasal Epithelia without Blocking Immune Responses
- (2008) P. L. Sinn et al. JOURNAL OF VIROLOGY
- CpG-free plasmids confer reduced inflammation and sustained pulmonary gene expression
- (2008) Stephen C Hyde et al. NATURE BIOTECHNOLOGY
Discover Peeref hubs
Discuss science. Find collaborators. Network.
Join a conversationBecome a Peeref-certified reviewer
The Peeref Institute provides free reviewer training that teaches the core competencies of the academic peer review process.
Get Started