Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells
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Title
Evaluation of Therapeutic Oligonucleotides for Familial Amyloid Polyneuropathy in Patient-Derived Hepatocyte-Like Cells
Authors
Keywords
Cell differentiation, Hepatocytes, Urine, Small interfering RNAs, Cell cultures, Induced pluripotent stem cells, Gene expression, Oligonucleotides
Journal
PLoS One
Volume 11, Issue 9, Pages e0161455
Publisher
Public Library of Science (PLoS)
Online
2016-09-02
DOI
10.1371/journal.pone.0161455
References
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