AAVrh10 vector corrects pathology in animal models of GM1 gangliosidosis and achieves widespread distribution in the CNS of nonhuman primates
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Title
AAVrh10 vector corrects pathology in animal models of GM1 gangliosidosis and achieves widespread distribution in the CNS of nonhuman primates
Authors
Keywords
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Journal
Molecular Therapy-Methods & Clinical Development
Volume 27, Issue -, Pages 281-292
Publisher
Elsevier BV
Online
2022-10-08
DOI
10.1016/j.omtm.2022.10.004
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