A single injection of an optimized AAV vector into cerebrospinal fluid corrects neurological disease in a murine model of GM1 gangliosidosis

Title
A single injection of an optimized AAV vector into cerebrospinal fluid corrects neurological disease in a murine model of GM1 gangliosidosis
Authors
Keywords
-
Journal
HUMAN GENE THERAPY
Volume -, Issue -, Pages -
Publisher
Mary Ann Liebert Inc
Online
2020-10-13
DOI
10.1089/hum.2018.206

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