Combined overexpression of ATXN1L and mutant ATXN1 knockdown by AAV rescue motor phenotypes and gene signatures in SCA1 mice
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Title
Combined overexpression of ATXN1L and mutant ATXN1 knockdown by AAV rescue motor phenotypes and gene signatures in SCA1 mice
Authors
Keywords
spinocerebellar ataxia type 1, ataxin-1, ataxin-1-like, AAV, miRNA, RNAi, cerebellum, neurodegeneration
Journal
Molecular Therapy-Methods & Clinical Development
Volume 25, Issue -, Pages 333-343
Publisher
Elsevier BV
Online
2022-04-13
DOI
10.1016/j.omtm.2022.04.004
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