Efficient suppression of endogenous CFTR nonsense mutations using anticodon-engineered transfer RNAs
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Title
Efficient suppression of endogenous CFTR nonsense mutations using anticodon-engineered transfer RNAs
Authors
Keywords
MT: Oligonucleotides: Therapies and Applications, nonsense suppressor tRNA, cystic fibrosis, CFTR, nonsense mutation, premature termination codon, nonsense-mediated decay, nonsense therapy
Journal
Molecular Therapy-Nucleic Acids
Volume 28, Issue -, Pages 685-701
Publisher
Elsevier BV
Online
2022-05-04
DOI
10.1016/j.omtn.2022.04.033
References
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