Impact of intracerebroventricular enzyme replacement therapy in patients with neuronopathic mucopolysaccharidosis type II
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Title
Impact of intracerebroventricular enzyme replacement therapy in patients with neuronopathic mucopolysaccharidosis type II
Authors
Keywords
heparan sulfate, idursulfase beta, infusions, intracerebroventricular, mucopolysaccharidosis II, pediatrics, psychology, developmental age, Kyoto Scale of Psychological Development 2001 (KSPD), enzyme replacement therapy
Journal
Molecular Therapy-Methods & Clinical Development
Volume 21, Issue -, Pages 67-75
Publisher
Elsevier BV
Online
2021-02-27
DOI
10.1016/j.omtm.2021.02.018
References
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