Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial

Title
Iduronate-2-Sulfatase with Anti-human Transferrin Receptor Antibody for Neuropathic Mucopolysaccharidosis II: A Phase 1/2 Trial
Authors
Keywords
mucopolysaccharidosis II, Hunter syndrome, blood brain barrier, iduronate-2-sulfatase, CNS, cognitive impairment, anti-human transferrin receptor antibody, heparan sulfate, dermatan sulfate, enzyme-replacement therapy, clinical trial
Journal
MOLECULAR THERAPY
Volume -, Issue -, Pages -
Publisher
Elsevier BV
Online
2018-12-08
DOI
10.1016/j.ymthe.2018.12.005

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