Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil
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Title
Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II: A phase 2 trial in Brazil
Authors
Keywords
mucopolysaccharidosis II, Hunter syndrome, pabinafusp alfa, JR-141, blood-brain barrier, iduronate-2-sulfatase, neurocognitive impairment, anti-human transferrin receptor antibody, heparan sulfate, enzyme-replacement therapy
Journal
MOLECULAR THERAPY
Volume -, Issue -, Pages -
Publisher
Elsevier BV
Online
2021-03-27
DOI
10.1016/j.ymthe.2021.03.019
References
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