Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation
出版年份 2020 全文链接
标题
Ex Vivo Gene Therapy Treats Bone Complications of Mucopolysaccharidosis Type II Mouse Models through Bone Remodeling Reactivation
作者
关键词
mucopolysaccharidosis type II, bone lineage, bone mineral density, bone strength, ex vivo, gene therapy, lentivirus, hematopoietic stem cell, Hunter disease, osteoclast, osteoblast
出版物
Molecular Therapy-Methods & Clinical Development
Volume 19, Issue -, Pages 261-274
出版商
Elsevier BV
发表日期
2020-09-20
DOI
10.1016/j.omtm.2020.09.012
参考文献
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