A gene therapy for inherited blindness using dCas9-VPR–mediated transcriptional activation
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Title
A gene therapy for inherited blindness using dCas9-VPR–mediated transcriptional activation
Authors
Keywords
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Journal
Science Advances
Volume 6, Issue 34, Pages eaba5614
Publisher
American Association for the Advancement of Science (AAAS)
Online
2020-08-20
DOI
10.1126/sciadv.aba5614
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