Antisense Oligonucleotide Reverses Leukodystrophy in Canavan Disease Mice
Published 2020 View Full Article
- Home
- Publications
- Publication Search
- Publication Details
Title
Antisense Oligonucleotide Reverses Leukodystrophy in Canavan Disease Mice
Authors
Keywords
-
Journal
ANNALS OF NEUROLOGY
Volume 87, Issue 3, Pages 480-485
Publisher
Wiley
Online
2020-01-11
DOI
10.1002/ana.25674
References
Ask authors/readers for more resources
Related references
Note: Only part of the references are listed.- Megalencephalic leukoencephalopathy with subcortical cysts: A personal biochemical retrospective
- (2018) Raúl Estévez et al. European Journal of Medical Genetics
- Two breakthrough gene-targeted treatments for spinal muscular atrophy: challenges remain
- (2018) Charlotte J. Sumner et al. JOURNAL OF CLINICAL INVESTIGATION
- Brain Nat8l Knockdown Suppresses Spongiform Leukodystrophy in an Aspartoacylase-Deficient Canavan Disease Mouse Model
- (2018) Peter Bannerman et al. MOLECULAR THERAPY
- Therapeutic Oligonucleotides: State of the Art
- (2018) C.I. Edvard Smith et al. Annual Review of Pharmacology and Toxicology
- Antisense Oligonucleotides: Translation from Mouse Models to Human Neurodegenerative Diseases
- (2017) Kathleen M. Schoch et al. NEURON
- Suppressing N -Acetyl-l-Aspartate Synthesis Prevents Loss of Neurons in a Murine Model of Canavan Leukodystrophy
- (2016) Jiho Sohn et al. JOURNAL OF NEUROSCIENCE
- Non-genetic therapeutic approaches to Canavan disease
- (2016) Rebecca B. Roscoe et al. JOURNAL OF THE NEUROLOGICAL SCIENCES
- Ablating N-acetylaspartate prevents leukodystrophy in a Canavan disease model
- (2015) Fuzheng Guo et al. ANNALS OF NEUROLOGY
- N-Acetylaspartate Synthase Deficiency Corrects the Myelin Phenotype in a Canavan Disease Mouse Model But Does Not Affect Survival Time
- (2015) H. Maier et al. JOURNAL OF NEUROSCIENCE
- A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice
- (2013) Seemin Seher Ahmed et al. MOLECULAR THERAPY
- Decreased NAA in Gray Matter is Correlated with Decreased Availability of Acetate in White Matter in Postmortem Multiple Sclerosis Cortex
- (2013) S. Li et al. NEUROCHEMICAL RESEARCH
- Canavan disease, a rare early-onset human spongiform leukodystrophy: Insights into its genesis and possible clinical interventions
- (2012) M.H. Baslow et al. BIOCHIMIE
- Long-Term Follow-Up After Gene Therapy for Canavan Disease
- (2012) P. Leone et al. Science Translational Medicine
- Aspartoacylase-LacZ Knockin Mice: An Engineered Model of Canavan Disease
- (2011) Nadine Mersmann et al. PLoS One
- Molecular identification of aspartate N-acetyltransferase and its mutation in hypoacetylaspartia
- (2009) Elsa Wiame et al. BIOCHEMICAL JOURNAL
- Nur7 Is a Nonsense Mutation in the Mouse Aspartoacylase Gene That Causes Spongy Degeneration of the CNS
- (2008) M. Traka et al. JOURNAL OF NEUROSCIENCE
Add your recorded webinar
Do you already have a recorded webinar? Grow your audience and get more views by easily listing your recording on Peeref.
Upload NowBecome a Peeref-certified reviewer
The Peeref Institute provides free reviewer training that teaches the core competencies of the academic peer review process.
Get Started