Advances in Sphingolipidoses: CRISPR-Cas9 Editing as an Option for Modelling and Therapy
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Title
Advances in Sphingolipidoses: CRISPR-Cas9 Editing as an Option for Modelling and Therapy
Authors
Keywords
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Journal
INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
Volume 20, Issue 23, Pages 5897
Publisher
MDPI AG
Online
2019-11-25
DOI
10.3390/ijms20235897
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