Genetic neuromuscular disorders: living the era of a therapeutic revolution. Part 1: peripheral neuropathies
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Title
Genetic neuromuscular disorders: living the era of a therapeutic revolution. Part 1: peripheral neuropathies
Authors
Keywords
Hereditary transthyretin amyloidosis, Inotersen, Patisiran, Charcot–Marie–Tooth disease, Acute intermittent porphyria, Mitochondrial neurogastrointestinal encephalomyopathy
Journal
NEUROLOGICAL SCIENCES
Volume -, Issue -, Pages -
Publisher
Springer Nature
Online
2019-03-07
DOI
10.1007/s10072-019-03778-7
References
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