Antisense oligonucleotide mediated therapy of spinal muscular atrophy
Published 2013 View Full Article
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Title
Antisense oligonucleotide mediated therapy of spinal muscular atrophy
Authors
Keywords
Antisense oligonucleotide, Splicing, ISS-N1, ASO, SMA, SMN, PMO, MOE
Journal
Translational Neuroscience
Volume 4, Issue 1, Pages 1-7
Publisher
Walter de Gruyter GmbH
Online
2013-03-06
DOI
10.2478/s13380-013-0109-2
References
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