Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector
Published 2018 View Full Article
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Title
Mutation-independent rhodopsin gene therapy by knockdown and replacement with a single AAV vector
Authors
Keywords
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Journal
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
Volume 115, Issue 36, Pages E8547-E8556
Publisher
Proceedings of the National Academy of Sciences
Online
2018-08-21
DOI
10.1073/pnas.1805055115
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